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Open Access 01-12-2014 | Oral presentation

Understanding off-label use and the new challenges

Author: Marc Dooms

Published in: Orphanet Journal of Rare Diseases | Special Issue 1/2014

Excerpt

As there are several thousands of rare disorders and only some tents of orphan drugs authorized in Europe, off-label use of medicinal products occurs frequently in the diagnosis, prevention and treatment of rare diseases. …

Title: Understanding off-label use and the new challenges
Author: Marc Dooms
Publication date: 01-12-2014
Publisher: BioMed Central
Published in: Orphanet Journal of Rare Diseases / Issue Special Issue 1/2014
Electronic ISSN: 1750-1172
DOI: https://doi.org/10.1186/1750-1172-9-S1-O22

At a glance: The ONWARDS insulin icodec trials

Springer Medicine

Understanding off-label use and the new challenges

Excerpt

At a glance: The ONWARDS insulin icodec trials

Springer Medicine

Excerpt

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