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Open Access 01-12-2014 | Oral presentation

The Biopontis Alliance Rare Disease Foundation (BARDF) – an innovative model for early stage rare disease therapy financing and development

Authors: Erik T Tambuyzer, Barbara L Handelin, Richard A Basile, Marlene E Haffner

Published in: Orphanet Journal of Rare Diseases | Special Issue 1/2014

Excerpt

The right therapy for the right patient at the right time is the most important approach for the provision of proper health care. The field of rare diseases is an excellent example, with patients taking a more central role in the discovery and development of treatments for their disease. Limited budgets coupled with high failure rates of medicine development lead us to public-private partnerships as a model to move forward and reduce cost; no stakeholder alone has all knowledge and expertise. …

Title: The Biopontis Alliance Rare Disease Foundation (BARDF) – an innovative model for early stage rare disease therapy financing and development
Authors: Erik T Tambuyzer
Barbara L Handelin
Richard A Basile
Marlene E Haffner
Publication date: 01-12-2014
Publisher: BioMed Central
Published in: Orphanet Journal of Rare Diseases / Issue Special Issue 1/2014
Electronic ISSN: 1750-1172
DOI: https://doi.org/10.1186/1750-1172-9-S1-O18

At a glance: The STEP trials

Springer Medicine

The Biopontis Alliance Rare Disease Foundation (BARDF) – an innovative model for early stage rare disease therapy financing and development

Excerpt

At a glance: The STEP trials

Springer Medicine

Excerpt

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German approach of coding rare diseases with ICD-10-GM and Orpha numbers in routine settings

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