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Published in: Annals of Hematology 10/2009

01-10-2009 | Review Article

The use of desmopressin in congenital factor XI deficiency: a systematic review

Authors: Massimo Franchini, Franco Manzato, Gian Luca Salvagno, Martina Montagnana, Giuseppe Lippi

Published in: Annals of Hematology | Issue 10/2009

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Abstract

Factor XI (FXI) deficiency is a rare inherited coagulation disorder characterized by infrequent spontaneous bleeding, but increased risk of hemorrhagic complications especially after trauma or surgery. Treatment options for FXI-deficient patients include virus-inactivated fresh frozen plasma, plasma-derived FXI concentrates, and activated recombinant FVII. Inhibitors of fibrinolysis, such as tranexamic acid, and desmopressin (DDAVP) have also been used in these patients, especially in mild cases. The current knowledge on the use of the latter agent in this congenital bleeding condition is systematically reviewed here. Although limited, the available literature data suggest the potential role of DDAVP for either treatment of bleeding episodes or the prevention of postoperative bleeding in patients with milder FXI defects. However, these findings need to be supported by further trials on large population of patients.
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Metadata
Title
The use of desmopressin in congenital factor XI deficiency: a systematic review
Authors
Massimo Franchini
Franco Manzato
Gian Luca Salvagno
Martina Montagnana
Giuseppe Lippi
Publication date
01-10-2009
Publisher
Springer-Verlag
Published in
Annals of Hematology / Issue 10/2009
Print ISSN: 0939-5555
Electronic ISSN: 1432-0584
DOI
https://doi.org/10.1007/s00277-009-0792-9

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