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Orphanet Journal of Rare Diseases
Published in: Orphanet Journal of Rare Diseases 1/2014

Open Access 01-12-2014 | Oral presentation

Early access to medicinal products: potential and limits

Author: Pauline J Evers

Published in: Orphanet Journal of Rare Diseases | Special Issue 1/2014

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Excerpt

On average it takes 12 years and a billion euros to develop a new medicinal product from first discovery to availability for patients. Especially in the later stages of development, when promising phase 2 data are available it is difficult to accept for patients there is no general access. In order to make medicines available at an earlier stage and to optimise their development, new ways of taking medicines through the assessment procedures for registration and reimbursement are highly needed. …
Literature
1.
Eichler HG, Oye K, Baird LG, et al: Adaptive licensing: taking the next step in the evolution of drug approval. Clinical Pharmacology & Therapeutics. 2012, 91 (3): 426-437. 10.1038/clpt.2011.345.CrossRef
2.
Metadata
Title
Early access to medicinal products: potential and limits
Author
Pauline J Evers
Publication date
01-12-2014
Publisher
BioMed Central
Published in
Orphanet Journal of Rare Diseases / Issue Special Issue 1/2014
Electronic ISSN: 1750-1172
DOI
https://doi.org/10.1186/1750-1172-9-S1-O24

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