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Metadata
Title
Spinal muscular atrophy: A test case for drug development in orphan diseases
Author
Lisa J. Bain
Publication date
01-10-2006
Publisher
Springer-Verlag
Published in
Neurotherapeutics / Issue 4/2006
Print ISSN: 1933-7213
Electronic ISSN: 1878-7479
DOI
https://doi.org/10.1016/j.nurx.2006.07.001

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