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Published in: Pediatric Rheumatology 1/2010

Open Access 01-12-2010 | Case Report

Effect of anakinra on arthropathy in CINCA/NOMID syndrome

Authors: Takako Miyamae, Yutaka Inaba, Gen Nishimura, Masako Kikuchi, Takayuki Kishi, Ryoki Hara, Utako Kaneko, Toshihiko Shinoki, Tomoyuki Imagawa, Shumpei Yokota

Published in: Pediatric Rheumatology | Issue 1/2010

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Abstract

CINCA/NOMID is an autoinflammatory disorder characterized by the triad of neonatal onset of cutaneous symptoms, chronic meningitis, and recurrent fever and it presents with distinctive osteoarthropathy, synovitis mainly of the large joints and overgrowth of epimetaphyseal cartilage, particularly of the long bones. The cartilage overgrowth eventually causes osseous overgrowth and deformity that persists beyond skeletal maturity and leads to limb length discrepancy, joint contracture, and early degenerative arthropathy. Autoinflammation in CAPS/NOMID has been proven to derive from excessive release of interleukin-1 (IL-1). It has been well documented that the IL-1 receptor antagonist anakinra (Kineret(R)) helps mitigate systemic inflammation in the disorder. However, a general consensus has not been reached on its beneficial effect on osteoarthropathy. The case of a girl with CINCA/NOMID syndrome who showed dramatic improvement of osteoarthropathy after anakinra treatment is reported. A 4-year-old girl suffered at the age of 10 months from a generalized urticarial skin lesion with recurrent episodes of fever and growth disorder. Blood examination revealed persistent massive neutrophilia, anemia and intense acute phase response. She manifested knee joint swelling with limited ROM when she was 20 months old and was diagnosed as being CINCA/NOMID based on characteristic findings of radiograph despite negative CIAS1 mutation. Radiological examination demonstrated metaphyseal fraying and cupping and widening of the growth plate in the distal femur. MR imaging showed mottled gadolinium enhancement at the chondrosseous junction. Neither significant joint effusion nor synovitis was identified. At 2 years and 7 months of age, anakinra, 2 mg/kg/day given by regular daily subcutaneous injections, was started. A few days after the initiation of the treatment, her clinical symptoms and laboratory findings of active inflammation were promptly alleviated. She was not able to walk unaided prior to the treatment, but she walked independently 1 month after the treatment. Follow-up radiographs and MR imaging showed that growth plate widening and gadolinium enhancement at the chondrosseous junction were less conspicuous. Furthermore, longitudinal growth of the femur and tibia was identified during 20 months of observation.
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Metadata
Title
Effect of anakinra on arthropathy in CINCA/NOMID syndrome
Authors
Takako Miyamae
Yutaka Inaba
Gen Nishimura
Masako Kikuchi
Takayuki Kishi
Ryoki Hara
Utako Kaneko
Toshihiko Shinoki
Tomoyuki Imagawa
Shumpei Yokota
Publication date
01-12-2010
Publisher
BioMed Central
Published in
Pediatric Rheumatology / Issue 1/2010
Electronic ISSN: 1546-0096
DOI
https://doi.org/10.1186/1546-0096-8-9

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