Issue 6/2024
Content (10 Articles)
Optimising Paediatric HIV Treatment: Recent Developments and Future Directions
- Open Access
- Lenacapavir
- Current Opinion
Anne E. M. Kamphuis, Alasdair Bamford, Alfredo Tagarro, Tim R. Cressey, Adrie Bekker, Pauline Amuge, Hilda Angela Mujuru, Francis Ateba Ndongo, Aminata Diack, Alexandra Compagnucci, Marc Lallemant, Angela Colbers, Anna Turkova
Recent Developments in the Treatment of Pediatric Distal Renal Tubular Acidosis
- Acidosis
- Leading Article
Olivia Boyer, Mélissa Ould Rabah, Evgenia Preka
Preventing Recurrence of Crohn’s Disease Post-Ileocaecal Surgery in Paediatric Patients: A Therapy Guide Based on Systematic Review of the Evidence
- Crohn's Disease
- Systematic Review
Jiri Bronsky, Kristyna Zarubova, Michal Kubat, Vojtech Dotlacil
Role of mTOR Inhibitors in Pediatric Liver Transplant Recipients: A Systematic Review
- mTOR-Inhibitors
- Systematic Review
Marjan Moghadamnia, Simin Dashti-Khavidaki, Hosein Alimadadi
Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy: A Systematic Review
- Duchenne Muscular Dystrophy
- Systematic Review
Carlos Pascual-Morena, Maribel Lucerón-Lucas-Torres, Irene Martínez-García, Eva Rodríguez-Gutiérrez, Silvana Patiño-Cardona, Irene Sequí-Domínguez
Pediatric Chronic Inflammatory Demyelinating Polyneuropathy: Challenges in Diagnosis and Therapeutic Strategies
- Polyneuropathy
- Review Article
Issa Alawneh, Asmaa Alenizi, Freddy Paiz, Elisa Nigro, Jiri Vajsar, Hernan Gonorazky
Targeted Treatments for Myasthenia Gravis in Children and Adolescents
- Myasthenia Gravis
- Review Article
Sithara Ramdas, Teresa Painho, Maria I. Vanegas, Dennis T. Famili, Ming J. Lim, Heinz Jungbluth
Clinical Evidence Supporting FDA Approval of Gene and RNA Therapies for Rare Inherited Conditions
- Duchenne Muscular Dystrophy
- Original Research Article
Ilina C. Odouard, Jeromie Ballreich, Branden Lee, Mariana P. Socal
The Effect of Levetiracetam and Valproic Acid Treatment on Anger and Attention Deficit Hyperactivity Disorder Clinical Features in Children and Adolescents with Epilepsy: A Prospective Study
- Attention Deficit Hyperactivity Disorder
- Original Research Article
Zeynep Vatansever Pınar, Safiye Güneş Sağer, İrem Damla Çimen, Yakup Çağ
Adverse Event Profile of First-line Drugs for Treating Patent Ductus Arteriosus in Neonates: A Disproportionality Analysis Study of USFDA Adverse Event Reporting System
- Patent Ductus Arteriosus
- Original Research Article
Kannan Sridharan, Gowri Sivaramakrishnan