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Successful Long-Term Enzyme Replacement Therapy in a Patient with Delayed-Onset ADA Deficiency

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Excerpt

To the Editor …
Title
Successful Long-Term Enzyme Replacement Therapy in a Patient with Delayed-Onset ADA Deficiency
Authors
Vasil Toskov
Pawan Bali
Michael S. Hershfield
Stephan Ehl
Carsten Speckmann
Publication date
01-12-2025
Publisher
Springer US
Keyword
Gene Therapy
Published in
Journal of Clinical Immunology / Issue 1/2025
Print ISSN: 0271-9142
Electronic ISSN: 1573-2592
DOI
https://doi.org/10.1007/s10875-024-01794-7
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