Issue 4/2025
Content (22 Articles)
Motor Function and Safety of Nusinersen and Risdiplam in Asian Patients with Types 2–4 Spinal Muscular Atrophy (SMA): A Systematic Review and Meta-Analysis
- Spinal Muscular Atrophy
- Review
Xinran Zhao, Yihan Liao, Jingyu Zhao, Lin Zhu, Jun Liu, Min Zhang, Wei Li
Pulmonary Hypertension Associated with Interstitial Lung Disease (PH-ILD): Back to the Future
- Open Access
- Pulmonary Hypertension
- Review
Giordano Fiorentù, Nicol Bernardinello, Giacomo Giulianelli, Elisabetta Cocconcelli, Elisabetta Balestro, Paolo Spagnolo
Comparability of Randomized Controlled Trials Evaluating Pharmacological Interventions for Pemphigus Vulgaris and Pemphigus Foliaceus: A Systematic Mapping Review
- Pemphigus
- Review
Corinne Le Reun, Najeeda Yasmeen, Alexis E. Cullen, Laura Sawyer, Olga Ostrovskaya, Francesca Barion
Southeast Asian, African, and Middle East Expert Consensus on Structured Physical Activity—Dance, Exercise, and Sports
- Review
Sarita Bajaj, Madhur Verma, Hanjabam Barun Sharma, Kaushik Ramaiya, Silver Bahendeka, Sanjay Kalra
No-Transcatheter Aortic Valve Replacement (TAVR) Zones and Their Effect on Access to Care for Medicare Beneficiaries with Aortic Stenosis
- Open Access
- Aortic Valve Replacement
- Original Research
Guy David, Andrew J. Epstein, Jay Giri, Ashwin Nathan, Soumya G. Chikermane, Michael Ryan, Christin Thompson, Seth Clancy, Candace Gunnarsson
Liver-Kidney-Metabolic Health, Sex, and Menopause Impact Total Scores and Monovessel vs. Multivessel Coronary Artery Calcification
- Metabolic Dysfunction-Associated Steatotic Liver Disease
- Original Research
Kamran Bagheri Lankarani, Mohamad Jamalinia, Fatemeh Zare, Seyed Taghi Heydari, Ali Ardekani, Amedeo Lonardo
Surgical Outcomes of Baerveldt Glaucoma Implant Versus Ahmed Glaucoma Valve in Neovascular Glaucoma: A Retrospective Multicenter Study
- Open Access
- Glaucoma
- Original Research
Kentaro Iwasaki, Sachi Kojima, Ryotaro Wajima, Akira Matsuda, Koki Yoshida, Aika Tsutsui, Michihiro Kono, Miho Nozaki, Koji Namiguchi, Keisuke Nitta, Yusaku Miura, Toshihiro Inoue, Tomomi Higashide, Kyoko Ishida, Masaki Tanito, Masaru Inatani
LymphoTEC: a Retrospective Real-World Study on Lymphocyte Reconstitution After Lymphopenia in Patients with Multiple Sclerosis Treated with Dimethyl Fumarate in France
- Open Access
- Dimethyl Fumarate
- Original Research
Jérôme de Sèze, Pierre Labauge, Roland Liblau, Mikel Martinez, Thibault Moreau, Laurent Suchet, Patrick Vermersch, Sandra Vukusic, Guillaume Mathey, Laure Michel, Jonathan Ciron, Aurelie Ruet, Elisabeth Maillart, Helene Zephir, Caroline Papeix, Gilles Defer, Mikael Cohen, David Axel Laplaud, Eric Berger, Pierre Clavelou, Eric Thouvenot, Olivier Heinzlef, Jean Pelletier, Claire Giannesini, Olivier Casez, Bertrand Bourre, Abir Wahab, Laurent Magy, Jean-Philippe Camdessanché, Inès Doghri, Céline Labeyrie, Karolina Hankiewicz, Jean-Philippe Neau, Corinne Pottier, Pamela Dobay, Hanyue Li, Seth Levin, Marilyn Gros, Marta Ruiz, Fabien Rollot
Real-world Outcomes Following Biologic Initiation in US Patients with Chronic Rhinosinusitis with Nasal Polyps
- Open Access
- Bronchial Asthma
- Original Research
Anju Peters, Xiaohui Zhao, Aimee M. Near, Joseph Han, Joseph D. Spahn, Sze-jung S. Wu, Andrew W. Lindsley, Tham T. Le, Elizabeth J. Wang, Rifat Tuly, Inyoung Lee, Christopher S. Ambrose
Onset and Long-Term Maintenance of Optimal Itch Response in Adult Patients with Moderate-to-Severe Atopic Dermatitis Treated with Dupilumab: Post Hoc Analysis from Two Phase 3 Trials
- Open Access
- Dupilumab
- Original Research
Sonja Ständer, Gil Yosipovitch, Eric L. Simpson, Brian S. Kim, Kenji Kabashima, Diamant Thaçi, Martin Metz, Zhen Chen, Sandra Hagen, Mike Bastian
Astaxanthin (AstaReal®) Improved Acute and Chronic Digital Eye Strain in Children: A Randomized Double-Blind Placebo-Controlled Trial
- Original Research
Karen A. Hecht, Megha Marwah, Vincent Wood, Yasuhiro Nishida, Austin E. Bach, Jeffry Gerson, Milton M. Hom, Joerg Schnackenberg, Sonal Raote, Shalini Srivastava, Pankaj Negi, Eric Caston
Patient and Health Care Professional Perspectives on the Burden and Daily Life Impact of Ulcerative Colitis and Crohn’s Disease: Results from the Japanese CONFIDE Study
- Open Access
- Ulcerative Colitis
- Original Research
Toshifumi Hibi, Taku Kobayashi, Masaru Tanaka, Satoshi Osaga, Alison J. Potts Bleakman, Theresa Hunter Gibble, Marijana Nedeljkovic Protic, Isabel Redondo, Koji Matsuo, Tadakazu Hisamatsu
Population Pharmacokinetics of Niraparib/Abiraterone Acetate Administered as Single-Agent Combination and Dual-Acting Tablets Plus Prednisone for Metastatic Castration-Resistant Prostate Cancer
- Prostate Cancer
- Original Research
Alberto Russu, Anasuya Hazra, Hui Tian, Nahor Haddish-Berhane, Juan Jose Perez Ruixo, Muriel Boulton
Application of a Value Framework to Determine the Value of Prophylaxis Versus On-Demand Treatment in Adults with Hemophilia A in China
- Hemophilia
- Original Research
Baoying Tan, Ailing Lin, Rong Han, Lu Bai, Jing Sun, Shanlian Hu, Jianwei Xuan
First-Line Pembrolizumab Plus Chemotherapy for HER2-Negative Advanced Gastric Cancer: China Subgroup Analysis of the Randomized Phase 3 KEYNOTE-859 Study
- Open Access
- Cytostatic Therapy
- Original Research
Shukui Qin, Yuxian Bai, Jin Li, Hongming Pan, Suxia Luo, Yanli Qu, Feng Ye, Lin Yang, Tianshu Liu, Wei Li, Xi Chen, Jianwei Yang, Jieer Ying, Xiaoyan Lin, Lin Zhao, Xinjun Liang, Yixiang Mao, Run Guo, Yi Zuo, Sonal Bordia, Shouguo Li
Long-Term Experience with Luspatercept in Relapsed/Refractory Myelodysplastic Neoplasms: A Chinese Real-World Study
- Erythropoietin
- Original Research
Zhuxin Zhang, Leyu Wang, Ziwei Liu, Chen Yang, Miao Chen, Bing Han
Cardiovascular Risks and Survival with Abiraterone vs Enzalutamide in Chemotherapy-Naïve Metastatic Castration-Resistant Prostate Cancer in Germany: AVENGER Study
- Open Access
- Enzalutamide
- Original Research
Axel S. Merseburger, Eugen Dornstauder, Carsten-Henning Ohlmann, Armen Aprikian, Sophia Junker, Philipp Hahn, Andrew Chilelli, Matthias Stoelzel, Alexis Serikoff, Stefan G. Spitzer
Survey on the Initiation of Aripiprazole Once-Monthly via a Two-Injection Start in Adult Patients with Schizophrenia: Experience of European Healthcare Professionals
- Open Access
- Aripiprazole
- Original Research
Andrea Fagiolini, Karolina Leopold, Sofia Pappa, William J. Cottam, Joe Hickey, Olivia Rogerson, Murat Yildirim, Clodagh Beckham
Patient-Reported Outcomes for Patients with Previously Treated Small Cell Lung Cancer Receiving Tarlatamab: Results from the DeLLphi-301 Phase 2 Trial
- Open Access
- Lung Cancer
- Original Research
Horst-Dieter Hummel, Myung-Ju Ahn, Fiona Blackhall, Martin Reck, Hiroaki Akamatsu, Suresh S. Ramalingam, Hossein Borghaei, Melissa Johnson, Franziska Dirnberger, Kim Cocks, Shuang Huang, Sujoy Mukherjee, Luis Paz-Ares
Characterizing Patient Diversity via Healthcare Access Determinants: A New Approach for Measuring Improvements in Clinical Trial Diversity in the United States
- Open Access
- Original Research
Jeffrey Yu, Adrian Kielhorn, James Murdoch, Marcus Martin, Eddilisa Martin, Kelly McNeil-Posey, Barbara Mungin, Yiyi Xia, Wendy Erler, Nuwan C. Kurukulasuriya
Analysis of Real-World Progression and Insufficient Response Variables and Related Endpoints Among Patients with Non-Hodgkin Lymphoma
- Open Access
- Non-Hodgkin Lymphoma
- Original Research
Madeline Richey, Christina Fullerton, Qianyi Zhang, Tori Williams, Douglas Donnelly, Hannah C. Wise, Aaron Dolor, Niquelle Wadé, Kelly Magee
Biologic Treatment Adherence and Persistence in Patients with Palmoplantar Pustulosis: A Real-World, Claims-Based Study
- Open Access
- Brief Report
Steven R. Feldman, Ran Gao, Rhonda L. Bohn, Stephani Gray, Anouk Déruaz-Luyet, Jashin J. Wu
